New and Media

Media Release
March 18, 2021
Nationwide Children’s Hospital Affiliate Andelyn Biosciences Receives Significant Investment and Enters Into Strategic Partnership with Pall Corporation and Cytiva
Research
April 2, 2018
Recent applications of adeno-associated virus (AAV) mediated gene therapy have focused mainly on correcting recessively inherited diseases. But what about dominantly inherited disorders? It looks like AAV could be a delivery mechanism for treating those genetic disorders, too.
News
September 20, 2016
Sarepta Therapeutics announced yesterday that the FDA has granted accelerated approval for eteplirsen for the treatment of Duchenne muscular dystrophy...