News & Media

News
March 1, 2023
Andelyn Biosciences Board of Directors Announce New CEO
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Research
July 24, 2018
Preclinical Gene Therapy Study Shows Muscle Restoration in Charcot-Marie-Tooth Disease Model
Tests of NT-3 gene therapy on mouse models suggest potential to treat a host of muscle-wasting conditions.
Research
April 2, 2018
Can Gene Therapy Treat Dominantly Inherited Disorders?
Recent applications of adeno-associated virus (AAV) mediated gene therapy have focused mainly on correcting recessively inherited diseases. But what about dominantly inherited disorders? It looks like AAV could be a delivery mechanism for treating those genetic disorders, too.
News
September 20, 2016
Nationwide Children’s Hospital Leads Effort for Gene Therapy Treatment for Duchenne Muscular Dystrophy
Sarepta Therapeutics announced yesterday that the FDA has granted accelerated approval for eteplirsen for the treatment of Duchenne muscular dystrophy...